The three-day annual fundraising event celebrated a weekend of wine, benefiting efforts to cure Duchenne muscular dystrophy ...
Working with Parent Project Muscular Dystrophy and the Duchenne Registry on patient identification and trial awareness efforts ~15,000 children ...
Your muscles need continuous maintenance to stay strong and healthy. Duchenne muscular dystrophy (DMD) happens when there is a change in a person's genetic instructions that affects the production of ...
Andelyn Biosciences, a leading and patient-focused cell and gene therapy Contract Development and Manufacturing Organization (CDMO), announced today a partnership with Evolyra Therapeutics to ...
A mother's persistence helps revive an all-but-abandoned drug class and could aid her son and thousands of others with ...
Duchenne muscular dystrophy (DMD) is a genetic condition caused by a change, or mutation, in the DMD gene. This gene normally tells the body how to make dystrophin, a protein that helps protect ...
Emma Ciafaloni, MD, FAAN, dives into the latest developments in gene therapy for muscular dystrophies, focusing on Duchenne muscular dystrophy, and discusses challenges, genetic causes, and the ...
The 'Laugh with Aidono' fundraiser raises awareness of Duchenne muscle dystrophy while sharing laughter.
Brody is a 10-year-old from Victoria who is fighting the daily challenges of living with Duchenne muscular dystrophy. Dooley, ...
We hypothesize that Duchenne muscular dystrophy and autism spectrum disorder/pervasive developmental disorder co-occur with a greater than random frequency. In this study, we set out to reject the ...
The muscular dystrophies are commonly associated with cardiovascular complications, including cardiomyopathy and cardiac arrhythmias. These complications are caused by intrinsic defects in ...
Results that may be inaccessible to you are currently showing.
Hide inaccessible results